We Deliver First-in-Class Therapies

We are an clinical-stage pharmaceutical company creating first-in-class therapies designed to boost expression of therapeutic genes in diseased cells.

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Close up of RNA molecule

RNAa Technology:

RNAa (RNA activation) is a platform technology to selectively turn genes on by using short duplex RNA known as small activating RNA (saRNA).

RNAa is among the limited technologies capable of stimulating the production of targeted endogenous genes.

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Our Pipeline:
The Push for the Next
Generation of Therapeutics

Ractigen has a diverse pipeline covering previously undruggable diseases and monogenic disorders including oncology, neurological and neuromuscular disorders, and liver-related indications.  

The pipeline explores the boundaries of our technology and pushes for the next generation of RNAa therapeutics.  

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Meet Our Team

Our leadership comprises a unified team of experts in RNA research and drug development, including the pioneers of RNAa technology, specialists in nucleic acid chemistry, biotech entrepreneurs, and authorities in drug discovery.

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News

07/15/2026 in Company News, Homepage News, News Highlight, RAG-17

Ractigen Therapeutics Announces Landmark Publication in Nature Medicine Highlighting Unprecedented Preclinical Efficacy and Positive First-in-Human Clinical Data for RAG-17 in SOD1-ALS

— Peer-reviewed publication details RAG-17’s robust translation from "bench to bedside," validating the proprietary SCAD™…
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06/06/2026 in Company News, Homepage News, News Highlight

Ractigen Therapeutics Announces ADA 2026 Late-Breaking Presentation Highlighting saRNA as a New Frontier in Obesity Control

Breakthrough preclinical data demonstrate that LiCO-saUcp1 effectively turns white fat into calorie-burning brown fat, driving…
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04/21/2026 in Company News, Homepage News, News Highlight, RAG-17

Ractigen Therapeutics Presents Positive Phase I Data for RAG-17 in SOD1-ALS at the 2026 AAN Annual Meeting, Demonstrating 81% Reduction in Neurofilament Light Chain

— Single intrathecal dose of SCAD-siRNA therapeutic RAG-17 yields favorable safety profile and profound, durable…
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03/19/2026 in Company News, Homepage News, News Highlight, RAG-01

Ractigen Therapeutics Announces China NMPA IND Approval for Phase II Clinical Trial of saRNA Therapy RAG-01 in Non-Muscle Invasive Bladder Cancer

Nantong, China – March 19, 2026 – Ractigen Therapeutics, a pioneering clinical-stage biotechnology company developing innovative small…
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