Therapeutic Area
Program
Indication
Phase
Monogenetic rare diseases
Lead discovery
RAG-06
Spinal muscular atrophy (SMA)
IND Enabling Studies
RAG-05
Acute intermittent porphyria
Lead optimisation
RAG-12
Undisclosed hepatic target
Lead discovery
Oncology
Lead discovery
RAG-01
Bladder cancer
IND Enabling Studies
RAG-07
Liver cancer
Lead optimisation
RAG-02
Immunotherapy
Lead discovery
Skin conditions
Lead discovery
RAG-11
Anti-aging
Lead discovery
RAG-04
Undisclosed
Lead discovery
Liver diseases
Lead discovery
RAG-03
Coagulation disorder
Lead discovery
RAG-10
Liver injury
Lead discovery
Others
Lead discovery
RAG-09
Sensory condition
Lead discovery
RAG-1C
Eye Condition
IND Enabling Studies